Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The disease is chronic and begins in childhood. The life expectancy of affected ...

A new program from University of Alabama at Birmingham will bring an experimental exon-skipping therapy to certain patients with Duchenne MD.

Patients with the disease experience impaired mobility, heart and lung problems, and ultimately a shortened life expectancy. "Current gene therapy for Duchenne muscular dystrophy utilizes a truncated ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is linked ...

Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...