ACMG, NSGC, and others in the genetics community are monitoring whether the widely used online clinical genetics database ...

NEW YORK – The UK's National Institute for Health and Care Excellence (NICE) on Friday recommended that the National Health Service make AstraZeneca's AKT pathway inhibitor Truqap (capivasertib) with ...

On the heels of its acquisition by Ocuphire Pharma, Opus is planning next steps for its Leber congenital amaurosis type 5 ...

The 2018 accelerated approval of Vitrakvi was converted to full approval based on results from three trials in adult and pediatric patients.

The company expects early cohort data this year from the trial assessing the calpain-2-targeted antisense oligonucleotide therapy.

The FDA cleared the firm this week to begin a Phase I study of ALX2004 in EGFR-expressing solid tumors, which could start in a few months.

BrainStorm has attempted to gain market approval for NurOwn without success but remains committed to developing the cell therapy.

The recommendation was based on results from the Phase III THOR trial, which compared Balversa to chemotherapy.

Cardinal is using its own cyclotron installations to produce Gozellix for distribution across a range of US locations.

The biotech firm closed an oversubscribed Series C funding round, proceeds from which it will use to advance ATSN-201 and its ...