Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.
Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...
In a highly anticipated article, FDA officials Vinay Prasad, M.D., and Martin Makary, M.D., outlined a novel regulatory ...
In this interview, Dr. Kelemen discusses the advantages of lipid-based delivery systems and their potential to expand the ...
As a new €2 million gene therapy research project funded by APC and Research Ireland is announced, we speak with the project lead Prof Niall Barron about its potential and how Ireland is positioning ...
Clinical Trials Arena on MSN
FDA unveils new pathway to usher bespoke therapies to market
The “plausible mechanism pathway” will allow personalised drugs to reach the market sooner for patients with genetic diseases ...
2don MSN
Researchers use AI and genetics to identify early signs of a rare, life-threatening heart condition
At Mayo Clinic, cardiologists Peter Noseworthy, M.D., and John Giudicessi, M.D., Ph.D., are uncovering the earliest signs of ...
MeiraGTx Holdings plc stock surges after a major Eli Lilly partnership boosts funding and pipeline. Click for my updated look ...
1hon MSN
There are more than 100 autoimmune diseases, and they mostly strike women. Here’s what to know
What are called autoimmune diseases can affect just about every part of the body — and tens of millions of people. While most ...
Only a week after Beau Friesen was born, his parents knew something was wrong, but two years later, they still don't know ...
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