The FDA on Friday granted accelerated approval to elamipretide (Forzinity) as the first treatment for the ultra-rare Barth syndrome, which affects approximately 150 Americans. Elamipretide once-daily ...
Walker Burger always loved baseball, but attending the games of his favorite team, the Atlanta Braves, used to be a physical challenge. In fact, every form of exercise was difficult. Burger, 35, has a ...
The FDA has granted accelerated approval for the elamipretide injection, the first treatment for Barth syndrome in patients weighing at least 30 kg. Barth syndrome is a life threatening disease of the ...
Stealth BioTherapeutics has claimed FDA approval for Forzinity, the first treatment for ultra-rare disease Barth syndrome, just a few months after it was turned down by the regulator. Forzinity ...
What Is Forzinity, and Why Does It Matter? Forzinity (elamipretide) is the first medicine to receive accelerated approval from the FDA for improving muscle strength in people with Barth syndrome who ...
After a tumultuous journey filled with delays and rejection, the FDA has approved Stealth BioTherapeutics’ treatment for the ultrarare disease Barth syndrome, marking the peptide as the first therapy ...
The Broadway controversy over Andrew Barth Feldman‘s casting in “Maybe Happy Ending” has continued, and actor Constance Wu has called him out for accepting the role. Feldman has taken over the lead ...
A Colorado family is in a race against time to secure access to an experimental drug that's keeping their infant son alive. Gilbert Dryden was born with Barth syndrome -- an ultra-rare genetic ...
Andrew Barth Feldman joins Maybe Happy Ending on Broadway tonight. Prior to his debut in the Tony-winning Best Musical, the production has released a first look at Feldman in costume as "Oliver." See ...
Former NFL kicker Connor Barth has listed an $8.5 million home in Wilmington, North Carolina's Landfall community. The 7,435-square-foot home, dubbed "The Cypress House," features four bedrooms, five ...
Stealth BioTherapeutics is resubmitting its NDA for elamipretide after resolving FDA manufacturing concerns, seeking expedited approval for Barth Syndrome treatment. The small patient population for ...
Gilbert Dryden probably only has enough medication to get him through the end of October, his mother, Madison, figures. Seven-month-old Gilbert has a rare genetic condition called Barth syndrome, one ...
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